Indian pharmaceutical firms have initiated the production of medications for 4 rare diseases, significantly reducing costs of drugs.
Made in India Drugs for Rare Diseases
Medications: The manufacturing started for at least four conditions including Tyrosinemia Type 1, Gaucher’s Disease, Wilson’s Disease, and Dravet-Lennox Gastaut Syndrome. They are likely to become available in early 2024.
At present, medicines are available at the centres of excellence for rare diseases.
Government is looking at the feasibility of making it available at Jan Aushadhi stores.
PLI Scheme: The government is working on a production-linked incentive (PLI) scheme for these medicines and is also promoting research on indigenous therapies for these conditions.
Other Medications: Government also urged the industry to produce an oral solution for hydroxyurea.
It is needed for the treatment of children up to the age of 5 years suffering from sickle cell disease.
What is the Rare Disease?
World Health Organisation (WHO) defines rare disease as a lifelong disease or disorder with a prevalence of 1 or less, per 1000 population.
Common Rare Diseases: They include Haemophilia, Thalassemia, Sickle-cell Anaemia and Primary Immuno Deficiency in children, auto-immune diseases, Hirschsprung disease, and certain forms of muscular dystrophies.
Rare Disease in India: Around 6% to 8% of the Indian population is estimated to have a rare disease.
Rare Disease Policy: Ministry of Health and Family Welfare has formulated a National Policy for Treatment of Rare Diseases (NPTRD) in July, 2017.
The policy aims at lowering the incidence and prevalence of rare diseases based on anintegrated and comprehensive preventive strategy.
Comprehensive coverage with a concise format Integration of PYQ within the booklet Designed as per recent trends of Prelims questions हिंदी में भी उपलब्ध
Quick Revise Now ! UDAAN PRELIMS WALLAH
Comprehensive coverage with a concise format Integration of PYQ within the booklet Designed as per recent trends of Prelims questions हिंदी में भी उपलब्ध
<div class="new-fform">
</div>
Subscribe our Newsletter
Sign up now for our exclusive newsletter and be the first to know about our latest Initiatives, Quality Content, and much more.